The process of identifying a suitable drug target for any given disease (inherited or otherwise) can be an extremely long process; translational research, drug discovery and clinical trials all mean that identifying and issuing a treatment can take decades and a considerable amount of money.
The ‘Partnership for Cures’ program funds drug repurposing projects enabling so-called ‘orphan diseases’ to be treated with existing therapies, foregoing the lengthy clinical trial process and massive costs, since such products have already been rigorously tested and approved.
There are currently several projects in the pipeline evaluating possible‘re-purposed’ therapies for BHD Syndrome, making this an extremely exciting time.
www.BHDSyndrome.org – the primary reference site for anybody interested in BHD Syndrome
