gene therapy

NIH researchers develop eye drops that slow vision loss in animals

New Transplant Method Shows Promise as Accessible Cure for Sickle Cell Disease

Genetic therapy gives infants life-changing improvements in sight

AI Designs Complex Protein Structures Inspired by Viral Architecture

Light-induced gene therapy disables cancer cells’ energy center

New Gene Therapy Shows Unprecedented Heart Failure Recovery in Large Animal Study

Scientists Uncover Hidden Risks in CRISPR Gene Editing for Rare Immune Disease

Gene therapy halts progression of rare genetic condition in young boy

Treating rare skin diseases by transplanting healthy skin

Scientists identify ‘missing piece’ required for blood stem cell self-renewal

Medicated foam could make gene therapies more accessible

Engineered Virus Crosses Blood-Brain Barrier, Delivers Therapeutic Genes in Mice

Gene therapy relieves back pain, repairs damaged disc in mice

New Compound Unlocks Cancer Cells for Targeted Gene Therapy